Hematology
Paroxysmal Nocturnal Hemoglobinuria
Expert Roundtables Podcast: Management of Thrombosis Risk in Paroxysmal Nocturnal Hemoglobinuria
Overview
<p>Thrombosis remains a leading cause of morbidity and mortality in paroxysmal nocturnal hemoglobinuria (PNH). Complement inhibitors are the cornerstone of treatment for PNH, significantly lowering the risk of thrombotic events. As noted by our experts in today’s podcast, anticoagulation continues to play a critical role, particularly in the secondary prevention and management of acute thrombosis.</p>
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References
Chen Y, Meng X, Wang Y, Liu C, Fu R. Several implications for the pathogenesis and treatment of thrombosis in PNH patients according to multiomics analysis. J Transl Med. 2024;22(1):129. doi:10.1186/s12967-024-04936-y
Kokoris S, Polyviou A, Evangelidis P, et al. Thrombosis in paroxysmal nocturnal hemoglobinuria (PNH): from pathogenesis to treatment. Int J Mol Sci. 2024;25(22):12104. doi:10.3390/ijms252212104.
Szer J. Thrombosis on PNH: largely gone, but not forgotten. Blood. 2024;144(2):125-126. doi:10.1182/blood.2024024660.



